Amyloidosis, Familial
Showing 1 - 25 of 1,299
Amyloidosis, Hereditary Trial in Richmond (Registry)
Not yet recruiting
- Amyloidosis, Hereditary
- Registry
-
Richmond, VirginiaVirginia Commonwealth University
Jul 25, 2023
Prospective Evaluation of NfL as a Biomarker in ATTRv
Not yet recruiting
- Amyloidosis, Hereditary
- (no location specified)
May 18, 2023
Familial Amyloidosis Trial in Nice (Psyllium)
Recruiting
- Familial Amyloidosis
- Psyllium
-
Nice, Provence Alpes Cote d'Azur, FranceUniversity Hospital of Nice
Jul 1, 2022
Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR
Not yet recruiting
- Amyloidosis, Hereditary
- +4 more
-
New York, New York
- +2 more
Aug 3, 2022
RWE-based Treatment Patterns and Outcomes in CIDP
Not yet recruiting
- Chronic Inflammatory Demyelinating Polyneuropathy
- +2 more
- No intervention. Retrospective observation only.
-
Salford, United KingdomNorthern Care Alliance NHS Foundation Trust
Jul 7, 2023
Patients With hATTR With Polyneuropathy Treated With Patisiran
Not yet recruiting
- Transthyretin Amyloidosis
- Amyloidosis, Hereditary
- Six minutes walk test
-
Bordeaux, France
- +7 more
May 24, 2023
Hereditary Transthyretin Amyloidosis Trial in Roma (Assessment of disease biomarkers)
Recruiting
- Hereditary Transthyretin Amyloidosis
- Assessment of disease biomarkers
-
Roma, ID, ItalyFondazione Policlinico Universitario Agostino Gemelli IRCCS
Jun 26, 2023
Amyloidosis, Familial, Transthyretin Amyloidosis Trial in Worldwide (Patisiran)
Completed
- Amyloidosis, Familial
- Transthyretin Amyloidosis
-
Créteil, France
- +8 more
Nov 22, 2021
Early Detection of Neuropathy in ATTRv
Recruiting
- Hereditary Amyloidosis, Transthyretin-Related
- neurofilament light chain
- +2 more
-
Philadelphia, PennsylvaniaUniversity of Pennsylvania
Mar 25, 2022
Instestinal Microbiome of Transthyretin Amyloidosis
Recruiting
- Amyloidosis, Hereditary, Transthyretin-Related
- Microbial Colonization
- collection of stools for genetic analysis
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Sao Paulo, BrazilUniversity of Sao Paulo Medical School - The Heart Institute
Jan 17, 2022
Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy,
Recruiting
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- +2 more
- NTLA-2001
-
Paris, France
- +3 more
Nov 29, 2022
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy Trial (NTLA-2001, Placebo)
Not yet recruiting
- Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
- NTLA-2001
- Placebo
- (no location specified)
Nov 8, 2023
The Regional Scintigraphic DPD Uptake in Cardiac Transthyretin
Recruiting
- Transthyretin Amyloidosis
- 99mTc-DPD scintigraphy
- Collection of blood samples and echocardiography
-
Krakow, Lesser Poland, PolandDepartment of Cardiac and Vascular Diseases, John Paul II Hospit
Apr 14, 2023
Systemic Transthyretin Amyloidosis: Carpal Tunnel Syndrome
Recruiting
- Transthyretin Amyloidosis
- Carpal Tunnel Syndrome
- Synovial biopsy and Cardiac scintigraphy with [99mTc]Tc-DPD
-
Porto, PortugalCentro Hospitalar Universitário São João
Jan 12, 2023
Amyloid Neuropathies, Transthyretin Amyloidosis Trial in Marseille (Electrophysiological biomarkers, MRI biomarkers)
Completed
- Amyloid Neuropathies
- Transthyretin Amyloidosis
- Electrophysiological biomarkers
- MRI biomarkers
-
Marseille, Paca, FranceAssistance Publique Des Hopitaux de Marseille
Oct 2, 2022
Transthyretin Amyloidosis Trial in New York (I 124-Evuzamitide)
Recruiting
- Transthyretin Amyloidosis
- I 124-Evuzamitide
-
New York, New YorkColumbia University Irving Medical Center
Nov 23, 2022
Hereditary Transthyretin Amyloidosis Patients Included in
Completed
- Hereditary Transthyretin Amyloidosis (ATTRv)
- Polyneuropathy
-
Barcelona, Spain
- +2 more
Dec 23, 2022
Hereditary Transthyretin Amyloidosis
Recruiting
- Amyloidosis
- +6 more
-
Cleveland, OhioCleveland Clinic
Mar 11, 2022
Cerebral MRI Anomalies in Mutated Transthyretin Amyloidosis
Completed
- Transthyretin Amyloidosis
- No intervention,
-
Nîmes, FranceCHU de Nîmes
Sep 1, 2022
Long-Term Follow-Up (LTFU) of Subjects Dosed With NTLA-2001
Not yet recruiting
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- +2 more
-
Auckland, New Zealand
- +2 more
Jan 24, 2023
Transthyretin Amyloidosis, Heart Failure, Heart Failure, Diastolic Trial in Boston (99mTc-pyrophosphate Scintigraphy)
Recruiting
- Transthyretin Amyloidosis
- +3 more
- 99mTc-pyrophosphate Scintigraphy
-
Boston, MassachusettsMassachusetts General Hospital
Oct 11, 2022
Mixed Phenotype Hereditary Transthyretin Amyloidosis
Not yet recruiting
- Hereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed Phenotype
- (no location specified)
Dec 8, 2022
High Frequency Imaging in Cerebral Amyloid Angiopathy
Recruiting
- Cerebral Amyloid Angiopathy
- MR Imaging
-
Bonn, Germany
- +2 more
Nov 7, 2023
Cerebral Amyloid Angiopathy Trial in Leiden (Minocycline, Placebo)
Recruiting
- Cerebral Amyloid Angiopathy
- Minocycline
- Placebo
-
Leiden, NetherlandsLeiden University Medical Center
Dec 26, 2022
Hereditary Transthyretin Amyloidosis With Polyneuropthy Trial in Canada, United States (Blood samples for immunoglobulins, Blood
Recruiting
- Hereditary Transthyretin Amyloidosis With Polyneuropthy
- Blood samples for immunoglobulins
- +2 more
-
Rosedale, New York
- +3 more
Dec 19, 2022